A genetic safety net for muscular dystrophy
Research report (imported) 2025 - Max Planck Institute for Heart and Lung Research - W. G. Kerckhoff Institute
Summary
Cells are not always defenceless against gene mutations – they have a plan B. While this genetic resilience has long been underestimated, we are harnessing it to develop new treatments for rare diseases such as Duchenne muscular dystrophy.